90. 網膜色素変性症
[臨床試験数:103,薬物数:158(DrugBank:42),標的遺伝子数:52,標的パスウェイ数:107

Searched query = "Retinitis pigmentosa", "Rod dystrophy", "Rod-Cone Dystrophy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

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1 trial found
No.TrialIDDate_
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agemin
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PhaseCountries
1NCT04517149
(ClinicalTrials.gov)
June 9, 202014/8/20204D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP)An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR GeneX-Linked Retinitis PigmentosaBiological: 4D-125 IVT Injection;Other: Observational4D Molecular TherapeuticsNULLRecruiting18 YearsN/AMale37Phase 1;Phase 2United States