111. Congenital myopathy
7 clinical trials,   13 drugs   (DrugBank: 4 drugs),   1 drug target gene,   8 drug target pathways

Searched query = "Congenital myopathy", "Nemaline myopathy", "Central core disease", "Minicore myopathy", "Myotubular myopathy", "Centronuclear myopathy", "Congenital fiber-type disproportion myopathy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
1 trial found
No.TrialIDDate_
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Public_titleScientific_titleConditionInterventionPrimary_
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agemin
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PhaseCountries
1NCT02035501
(ClinicalTrials.gov)
January 20142/7/2013Treatment of TNNT1-Myopathy With L-Tyrosine.Treatment of TNNT1-Myopathy With L-Tyrosine. A Double-blind, Placebo-controlled Crossover Trial.Nemaline MyopathyDrug: L-Tyrosine;Drug: PlaceboHadassah Medical OrganizationNULLEnrolling by invitationN/A20 YearsBoth10Phase 2Israel