DDrare: Database of Drug Development for Rare Diseases

Searched query = "Hepatic glycogenosis", "Liver glycogenosis", "Hepatic glycogen storage disease", "Liver glycogen storage disease", "Glycogen storage disease type I", "GSDI", "von Gierke disease", "Glucose-6-phosphatase deficiency", "G6Pase deficiency", "Glycogen storage disease type III", "GSDIII", "Cori disease", "Glycogen debranching enzyme deficiency", "Glycogen storage disease type IV", "GSDIV", "Andersen disease", "Glycogen-branching enzyme deficiency", "GBED", "Adult polyglucosan body disease", "Glycogen storage disease type VI", "GSDVI", "Hers disease", "Hepatic phosphorylase deficiency", "Liver phosphorylase deficiency", "Glycogen storage disease type IX", "GSDIX", "Phosphorylase kinase deficiency"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Drug = Carbohydrates intake; Cornstarch; EPHYNAL; Empagliflozin; FAXE Kondi; Faxe Kondi Free; Glucose; Glucose intake; Glycosade; Other: Vegetable Oil; QUARK; Quark; Ramipril; Sweet polvilho; TRIHEPTANOIN; Tocopherol; Tocopherol (vit E); Triheptanoin; UX007

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03871673 (ClinicalTrials.gov)	April 29, 2017	9/3/2019	The Use of Uncooked Sweet Polvilho to Treat Hepatic Glycogen Storage Diseases	A Novel Approach to Treatment of Hepatic Glycogen Storage Diseases: a Study Based on the Use of Uncooked Sweet Polvilho	Glycogen Storage Disease Type I	Dietary Supplement: sweet polvilho;Dietary Supplement: Cornstarch	Hospital de Clinicas de Porto Alegre	Conselho Nacional de Desenvolvimento Científico e Tecnológico;Fundação Médica do Rio Grande do Sul	Active, not recruiting	16 Years	N/A	All	11	N/A	Brazil
2	NCT02054832 (ClinicalTrials.gov)	November 2013	31/1/2014	Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard Versus Modified Uncooked Cornstarch	A Comparison of Quality of Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard and Modified Uncooked Cornstarch	Glycogen Storage Disease Type IA;Glycogen Storage Disease Type IB;Glycogen Storage Disease Type III;Glycogen Storage Disease Type 0	Dietary Supplement: Glycosade	John Mitchell	NULL	Completed	2 Years	50 Years	Both	11	N/A	Canada

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT03871673
(ClinicalTrials.gov)

April 29, 2017

9/3/2019

The Use of Uncooked Sweet Polvilho to Treat Hepatic Glycogen Storage Diseases

A Novel Approach to Treatment of Hepatic Glycogen Storage Diseases: a Study Based on the Use of Uncooked Sweet Polvilho

Glycogen Storage Disease Type I

Dietary Supplement: sweet polvilho;Dietary Supplement: Cornstarch

Hospital de Clinicas de Porto Alegre

Conselho Nacional de Desenvolvimento Científico e Tecnológico;Fundação Médica do Rio Grande do Sul

Active, not recruiting

16 Years

N/A

All

N/A

Brazil

NCT02054832
(ClinicalTrials.gov)

November 2013

31/1/2014

Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard Versus Modified Uncooked Cornstarch

A Comparison of Quality of Sleep and Quality of Life in Patients With Glycogen Storage Disease on Standard and Modified Uncooked Cornstarch

Glycogen Storage Disease Type IA;Glycogen Storage Disease Type IB;Glycogen Storage Disease Type III;Glycogen Storage Disease Type 0

Dietary Supplement: Glycosade

John Mitchell

NULL

Completed

2 Years

50 Years

Both

N/A

Canada