Sodium 4-phenylbutyrate (4pba)    (DrugBank: 4-phenylbutyrate, Phenylbutyrate)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
299嚢胞性線維症1

299. 嚢胞性線維症 [臨床試験数:1,592,薬物数:1,539(DrugBank:255),標的遺伝子数:81,標的パスウェイ数:162
Searched query = "Cystic fibrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 1,592 trial found
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1NCT00016744
(ClinicalTrials.gov)
September 200131/5/2001Phenylbutyrate/Genistein Duotherapy in Delta F508-Homozygous(for Cystic Fibrosis)A Pilot Trial of Phenylbutyrate/Genistein Duotherapy in Delta F508-Homozygous Cystic Fibrosis PatientsCystic FibrosisDrug: Sodium 4-Phenylbutyrate (4PBA);Drug: Unconjugated Isoflavones 100 (PTI G-4660, 87% Genistein);Drug: PlaceboChildren's Hospital of PhiladelphiaCystic Fibrosis Foundation Therapeutics;National Center for Research Resources (NCRR)Completed18 YearsN/ABoth12Phase 1;Phase 2United States