DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
36	表皮水疱症	1

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01263379 (ClinicalTrials.gov)	October 5, 2010	15/12/2010	Gene Transfer for Recessive Dystrophic Epidermolysis Bullosa	A Phase 1/2A Single Center Trial of Gene Transfer for Recessive Dystrophic Epidermolysis Bullosa (RDEB) Using the Drug LZRSE-Col7A1 Engineered Autologous Epidermal Sheets (LEAES)	Epidermolysis Bullosa Dystrophica;Epidermolysis Bullosa	Biological: LZRSE-Col7A1 Engineered Autologous Epidermal Sheets	Stanford University	National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS);Abeona Therapeutics, Inc	Active, not recruiting	13 Years	N/A	All	10	Phase 1;Phase 2	United States

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT01263379
(ClinicalTrials.gov)

October 5, 2010

15/12/2010

Gene Transfer for Recessive Dystrophic Epidermolysis Bullosa

A Phase 1/2A Single Center Trial of Gene Transfer for Recessive Dystrophic Epidermolysis Bullosa (RDEB) Using the Drug LZRSE-Col7A1 Engineered Autologous Epidermal Sheets (LEAES)

Epidermolysis Bullosa Dystrophica;Epidermolysis Bullosa

Biological: LZRSE-Col7A1 Engineered Autologous Epidermal Sheets

Stanford University

National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS);Abeona Therapeutics, Inc

Active, not recruiting

13 Years

N/A

All

Phase 1;Phase 2

United States