Sapropterin dihydrochloride (6r-bh4) (DrugBank: Sapropterin, 6R-BH4)
5 diseases告示番号 | 疾患名(ページ内リンク) | 臨床試験数 |
---|---|---|
51 | 全身性強皮症 | 0 |
86 | 肺動脈性肺高血圧症 | 1 |
124 | 皮質下梗塞と白質脳症を伴う常染色体優性脳動脈症 | 0 |
240 | フェニルケトン尿症 | 0 |
299 | 嚢胞性線維症 | 0 |
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT00435331 (ClinicalTrials.gov) | March 2008 | 12/2/2007 | 6R-BH4 Pulmonary Arterial Hypertension Study | A Phase 1, Multicenter, Open-label, Dose-escalation Study to Evaluate the Safety and Efficacy of 6R-BH4 in Subjects With Pulmonary Arterial Hypertension | Pulmonary Arterial Hypertension | Drug: sapropterin dihydrochloride (6R-BH4) | Vanderbilt University | National Institutes of Health (NIH);BioMarin Pharmaceutical | Completed | 18 Years | N/A | Both | 14 | Phase 1 | United States |