DDrare: Database of Drug Development for Rare Diseases

Acetohydroxamic acid oral tablet [lithostat] (DrugBank: Acetohydroxamic acid)

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
6	パーキンソン病	0
251	尿素サイクル異常症	1

6. パーキンソン病　［臨床試験数：2,123，薬物数：2,046（DrugBank：324），標的遺伝子数：183，標的パスウェイ数：198］

Searched query = "Parkinson disease"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: . Trials are sorted by Date_enrollment from most recent to oldest in the table.

0 / 2,123 trial found

251. 尿素サイクル異常症　［臨床試験数：42，薬物数：45（DrugBank：10），標的遺伝子数：4，標的パスウェイ数：29］

Searched query = "Urea cycle disorder", "N-acetylglutamate synthase deficiency", "NAGS deficiency", "Carbamoyl phosphate synthetase I deficiency", "CPS1 deficiency", "Ornithine transcarbamylase deficiency", "OTC deficiency", "Classic citrullinemia", "Citrullinemia type I", "Argininosuccinic aciduria", "Argininemia", "Hiperornitinemia-hiperamonemia-homocitrulinuria syndrome", "HHH syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 42 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03181828 (ClinicalTrials.gov)	March 24, 2017	1/6/2017	Manipulating the Gut Microbiome Study	Manipulating the Gut Microbiome Study	Urea Cycle Disorder	Drug: Acetohydroxamic Acid Oral Tablet [Lithostat]	Nicholas Ah Mew	NULL	Terminated	18 Years	60 Years	All	4	Phase 1;Phase 2	United States