DDrare: Database of Drug Development for Rare Diseases

Procedure: sham (DrugBank: -)

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
90	網膜色素変性症	1
303	アッシャー症候群	1

90. 網膜色素変性症　［臨床試験数：103，薬物数：158（DrugBank：42），標的遺伝子数：52，標的パスウェイ数：107］

Searched query = "Retinitis pigmentosa", "Rod dystrophy", "Rod-Cone Dystrophy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 103 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01530659 (ClinicalTrials.gov)	January 2012	19/1/2012	Retinal Imaging of Subjects Implanted With Ciliary Neurotrophic Factor (CNTF)-Releasing Encapsulated Cell Implant for Early-stage Retinitis Pigmentosa	Photoreceptor Structure in A Phase 2 Study of Encapsulated Human NTC-201 Cell Implants Releasing Ciliary Neurotrophic Factor (CNTF) for Participants With Retinitis Pigmentosa Using Rates of Change in Cone Spacing and Density	Retinitis Pigmentosa;Usher Syndrome Type 2;Usher Syndrome Type 3	Drug: NT-501;Procedure: Sham	Neurotech Pharmaceuticals	University of California, San Francisco;FDA Office of Orphan Products Development	Unknown status	18 Years	55 Years	All	30	Phase 2	United States

303. アッシャー症候群　［臨床試験数：6，薬物数：11（DrugBank：0），標的遺伝子数：0，標的パスウェイ数：0］

Searched query = "Usher syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 6 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01530659 (ClinicalTrials.gov)	January 2012	19/1/2012	Retinal Imaging of Subjects Implanted With Ciliary Neurotrophic Factor (CNTF)-Releasing Encapsulated Cell Implant for Early-stage Retinitis Pigmentosa	Photoreceptor Structure in A Phase 2 Study of Encapsulated Human NTC-201 Cell Implants Releasing Ciliary Neurotrophic Factor (CNTF) for Participants With Retinitis Pigmentosa Using Rates of Change in Cone Spacing and Density	Retinitis Pigmentosa;Usher Syndrome Type 2;Usher Syndrome Type 3	Drug: NT-501;Procedure: Sham	Neurotech Pharmaceuticals	University of California, San Francisco;FDA Office of Orphan Products Development	Unknown status	18 Years	55 Years	All	30	Phase 2	United States