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Genetic: recombinant adenovirus containing the ornithine transcarbamylase gene    (DrugBank: Ornithine)

1 disease
IDDisease name (Link within this page)Number of trials
251Urea cycle disorder1

251. Urea cycle disorder    [ 42 clinical trials,   45 drugs,   (DrugBank: 10 drugs),   4 drug target genes,   29 drug target pathways]
Searched query = "Urea cycle disorder", "N-acetylglutamate synthase deficiency", "NAGS deficiency", "Carbamoyl phosphate synthetase I deficiency", "CPS1 deficiency", "Ornithine transcarbamylase deficiency", "OTC deficiency", "Classic citrullinemia", "Citrullinemia type I", "Argininosuccinic aciduria", "Argininemia", "Hiperornitinemia-hiperamonemia-homocitrulinuria syndrome", "HHH syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 42 trial found
No.TrialIDDate_
enrollment		Date_
registration		Public_titleScientific_titleConditionInterventionPrimary_
sponsor		Secondary_
sponsor		Recruitment_
Status		Inclusion_
agemin		Inclusion_
agemax		Inclusion_
gender		Target_
size		PhaseCountries
1NCT00004386
(ClinicalTrials.gov)		October 199518/10/1999Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseGenetic: recombinant adenovirus containing the ornithine transcarbamylase geneEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Children's Research InstituteTerminated18 Years65 YearsBothPhase 1NULL