DDrare: Database of Drug Development for Rare Diseases

Acetohydroxamic acid oral tablet [lithostat] (DrugBank: Acetohydroxamic acid)

2 diseases

ID	Disease name (Link within this page)	Number of trials
6	Parkinson disease	0
251	Urea cycle disorder	1

6. Parkinson disease [ 2,123 clinical trials, 2,046 drugs, (DrugBank: 324 drugs), 183 drug target genes, 198 drug target pathways]

Searched query = "Parkinson disease"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: . Trials are sorted by Date_enrollment from most recent to oldest in the table.

0 / 2,123 trial found

251. Urea cycle disorder [ 42 clinical trials, 45 drugs, (DrugBank: 10 drugs), 4 drug target genes, 29 drug target pathways]

Searched query = "Urea cycle disorder", "N-acetylglutamate synthase deficiency", "NAGS deficiency", "Carbamoyl phosphate synthetase I deficiency", "CPS1 deficiency", "Ornithine transcarbamylase deficiency", "OTC deficiency", "Classic citrullinemia", "Citrullinemia type I", "Argininosuccinic aciduria", "Argininemia", "Hiperornitinemia-hiperamonemia-homocitrulinuria syndrome", "HHH syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 42 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03181828 (ClinicalTrials.gov)	March 24, 2017	1/6/2017	Manipulating the Gut Microbiome Study	Manipulating the Gut Microbiome Study	Urea Cycle Disorder	Drug: Acetohydroxamic Acid Oral Tablet [Lithostat]	Nicholas Ah Mew	NULL	Terminated	18 Years	60 Years	All	4	Phase 1;Phase 2	United States