DDrare: Database of Drug Development for Rare Diseases

Npi-001 (DrugBank: -)

2 diseases

ID	Disease name (Link within this page)	Number of trials
90	Retinitis pigmentosa	1
303	Usher syndrome	1

90. Retinitis pigmentosa [ 103 clinical trials, 158 drugs, (DrugBank: 42 drugs), 52 drug target genes, 107 drug target pathways]

Searched query = "Retinitis pigmentosa", "Rod dystrophy", "Rod-Cone Dystrophy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 103 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04355689 (ClinicalTrials.gov)	September 3, 2020	17/4/2020	Safety and Efficacy of NPI-001 Tablets for RP Associated With Usher Syndrome	Safety and Efficacy of NPI-001 Tablets Versus Placebo for Treatment of Retinitis Pigmentosa Associated With Usher Syndrome	Usher Syndromes	Drug: NPI-001;Other: Placebo	Nacuity Pharmaceuticals, Inc.	Foundation Fighting Blindness	Recruiting	18 Years	N/A	All	48	Phase 1;Phase 2	Australia

303. Usher syndrome [ 6 clinical trials, 11 drugs, (DrugBank: 0), 0 drug target gene, 0 drug target pathway]

Searched query = "Usher syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 6 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04355689 (ClinicalTrials.gov)	September 3, 2020	17/4/2020	Safety and Efficacy of NPI-001 Tablets for RP Associated With Usher Syndrome	Safety and Efficacy of NPI-001 Tablets Versus Placebo for Treatment of Retinitis Pigmentosa Associated With Usher Syndrome	Usher Syndromes	Drug: NPI-001;Other: Placebo	Nacuity Pharmaceuticals, Inc.	Foundation Fighting Blindness	Recruiting	18 Years	N/A	All	48	Phase 1;Phase 2	Australia