19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03201627 (ClinicalTrials.gov)	July 5, 2017	26/6/2017	Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease	a Single-center, Prospective, Open, and Non-randomized Case-control Study of Lithium Carbonate Effect on Niemann Disease C1 Type	Niemann-Pick Disease, Type C1	Drug: Lithium Carbonate	Xinhua Hospital, Shanghai Jiao Tong University School of Medicine	NULL	Active, not recruiting	7 Years	40 Years	All	18	Early Phase 1	China
2	NCT00004488 (ClinicalTrials.gov)	October 1998	18/10/1999	Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease		Gaucher's Disease;Osteopenia	Drug: alendronate sodium;Drug: calcium carbonate;Drug: cholecalciferol	Children's Hospital Medical Center, Cincinnati	NULL	Completed	18 Years	50 Years	Both	82	Phase 2	United States;Israel