325. 遺伝性自己炎症疾患 Hereditary autoinflammatory syndrome Clinical trials / Disease details


臨床試験数 : 7 薬物数 : 16 - (DrugBank : 6) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 35

  
2 trials found
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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Inclusion_
agemin
Inclusion_
agemax
Inclusion_
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PhaseCountries
1NCT04731103
(ClinicalTrials.gov)
February 202214/7/2020Inhibition of Reverse Transcription in Type I Interferon Mediated NeuropathologyInhibition of Reverse Transcription in Type I Interferon Mediated NeuropathologyAicardi-Goutières SyndromeDrug: Abacavir (ABC);Drug: Lamivudine (3TC);Drug: Abacavir (ABC)+Lamivudine (3TC)+Zidovudine (AZT)University of EdinburghNHS Lothian;Medical Research CouncilNot yet recruiting3 Months15 YearsAll24Phase 2United Kingdom
2NCT02363452
(ClinicalTrials.gov)
September 10, 201515/1/2015Reverse Transcriptase Inhibitors in AGSA Pilot Clinical Trial of Reverse Transcriptase Inhibitors in Children With Aicardi-Goutières Syndrome (AGS)Aicardi-Goutières Syndrome (AGS)Drug: Reverse transcriptase inhibitors: Zidovudine, Lamivudine, AbacavirAssistance Publique - Hôpitaux de ParisNULLCompleted1 Month17 YearsAll11Phase 2France