18. Spinocerebellar degeneration Clinical trials / Disease details
Clinical trials : 71 / Drugs : 99 - (DrugBank : 30) / Drug target genes : 45 - Drug target pathways : 65
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04519567 (ClinicalTrials.gov) | July 31, 2020 | 17/8/2020 | Multiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | A Phase 1 Multiple Ascending Dose Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Subcutaneous CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | Friedreich Ataxia | Biological: CTI-1601;Biological: Placebo | Larimar Therapeutics, Inc. | Veristat, Inc.;Metrum Research Group, LLC | Completed | 18 Years | N/A | All | 27 | Phase 1 | United States |
| 2 | NCT04176991 (ClinicalTrials.gov) | December 11, 2019 | 14/11/2019 | Single Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | A Phase 1 Single Ascending Dose Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Subcutaneous CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia | Friedreich Ataxia | Biological: CTI-1601;Biological: Placebo | Larimar Therapeutics, Inc. | Veristat, Inc.;Metrum Research Group, LLC | Completed | 18 Years | N/A | All | 28 | Phase 1 | United States |