244. Maple syrup urine disease Clinical trials / Disease details
Clinical trial : 1 / Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT01529060 (ClinicalTrials.gov) | February 2013 | 6/2/2012 | Phenylbutyrate Therapy for Maple Syrup Urine Disease | A Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine Disease | Maple Syrup Urine Disease | Drug: Phenylbutyrate;Drug: Placebo powder | Brendan Lee | NULL | Completed | 3 Years | N/A | All | 20 | Phase 2/Phase 3 | United States |