284. Diamond-Blackfan anemia Clinical trials / Disease details


Clinical trials : 37 Drugs : 110 - (DrugBank : 34) / Drug target genes : 23 - Drug target pathways : 124

  
1 trial found
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1NCT02386267
(ClinicalTrials.gov)
September 201418/2/2015L-leucine in Diamond Blackfan Anemia PatientsTherapeutic Use of the Amino Acid Leucine in the Treatment of Transfusion-Dependent Diamond Blackfan Anemia PatientsDiamond Blackfan AnemiaDrug: L-leucineFederal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry RogacheNULLRecruiting1 Year20 YearsBoth30Phase 2Russian Federation