Other: Quality of life assessment ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
122脳表ヘモジデリン沈着症1

122. 脳表ヘモジデリン沈着症


臨床試験数 : 4 薬物数 : 9 - (DrugBank : 3) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04200664
(ClinicalTrials.gov)
February 7, 202010/12/2019Audiovestibular Function in Infratentorial Superficial SiderosisClinical and Imaging Biomarkers of Audiovestibular Function in Infratentorial Superficial SiderosisSiderosis;Neurological Disorder;Rare Diseases;Age Related Hearing Loss;PresbycusisDiagnostic Test: Hearing assessment;Diagnostic Test: Vestibular/balance assessment;Other: Quality of life assessment;Diagnostic Test: Olfactory (smell) function testing;Genetic: DNA bio-bankingUniversity College, LondonNIHR UCLH BRC;The Bernice Bibby Research TrustCompleted18 YearsN/AAll90United Kingdom