Natural History of Atypical Morquio A Disease: a 5-years Prospective Study in a Series of 9 Adult Patients Followed in a Single Expert Center Natural History of Atypical Morquio A Disease: a 5-years Prospective Study in a Series of 9 Adult Pa ...
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Mucopolysaccharidosis IV Type A;Morquio A Syndrome;MPS IVA
Drug: Vimizim® (elosulfase alfa)
BioMarin Pharmaceutical
ICON plc
Recruiting
N/A
N/A
All
583
United States;Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Ireland;Italy;Malaysia;Netherlands;Poland;Portugal;Puerto Rico;Taiwan;United Kingdom United States;Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Ireland;Italy;Malaysia ...