Crysvita (burosumab-twza) Treatment ( DrugBank: Burosumab, burosumab-twza )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
238ビタミンD抵抗性くる病/骨軟化症1

238. ビタミンD抵抗性くる病/骨軟化症


臨床試験数 : 29 薬物数 : 25 - (DrugBank : 11) / 標的遺伝子数 : 4 - 標的パスウェイ数 : 20
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agemin
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PhaseCountries
1NCT04320316
(ClinicalTrials.gov)
July 31, 202011/3/2020A Trial to Assess the Safety and Efficacy of KRN23 in Epidermal Nevus Syndrome (ENS)An Open Label Trial to Assess the Safety and Efficacy of KRN23, an Investigational Antibody to FGF23, in a Single Pediatric Patient With Epidermal Nevus Syndrome (ENS) and Associated Hypophosphatemic RicketsEpidermal Nevus SyndromeDrug: Crysvita (burosumab-twza) TreatmentUniversity of Alabama at BirminghamUltragenyx Pharmaceutical IncCompleted6 MonthsN/AMale1Phase 4United States