Genetic: recombinant adenovirus containing the ornithine transcarbamylase gene ( DrugBank: Ornithine )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
251尿素サイクル異常症1

251. 尿素サイクル異常症


臨床試験数 : 48 薬物数 : 52 - (DrugBank : 13) / 標的遺伝子数 : 4 - 標的パスウェイ数 : 29
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enrollment
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registration
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Inclusion_
agemin
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agemax
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PhaseCountries
1NCT00004386
(ClinicalTrials.gov)
October 199518/10/1999Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseGenetic: recombinant adenovirus containing the ornithine transcarbamylase geneEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Children's Research InstituteTerminated18 Years65 YearsBothPhase 1NULL