L-leucine ( DrugBank: Leucine, L-Leucine )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
284ダイアモンド・ブラックファン貧血1

284. ダイアモンド・ブラックファン貧血


臨床試験数 : 37 薬物数 : 110 - (DrugBank : 34) / 標的遺伝子数 : 23 - 標的パスウェイ数 : 124
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT02386267
(ClinicalTrials.gov)
September 201418/2/2015L-leucine in Diamond Blackfan Anemia PatientsTherapeutic Use of the Amino Acid Leucine in the Treatment of Transfusion-Dependent Diamond Blackfan Anemia PatientsDiamond Blackfan AnemiaDrug: L-leucineFederal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry RogacheNULLRecruiting1 Year20 YearsBoth30Phase 2Russian Federation