Haploidentical Hematopoietic Cell Transplantation ( DrugBank: - )


2 diseases
告示番号疾患名(ページ内リンク)臨床試験数
60再生不良性貧血1
65原発性免疫不全症候群1

60. 再生不良性貧血


臨床試験数 : 235 薬物数 : 381 - (DrugBank : 83) / 標的遺伝子数 : 44 - 標的パスウェイ数 : 160
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04356469
(ClinicalTrials.gov)
July 22, 202019/4/2020TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in ChildrenStudy of TCR Alpha Beta T-Cell and CD19 B-Cell Depletion for Hematopoietic Cell Transplantation From Haploidentical Donors in the Treatment of Non-Malignant Hematological Disorders in ChildrenHemoglobinopathy (Disorder);Severe Aplastic Anemia;Bone Marrow Failure SyndromeBiological: Haploidentical Hematopoietic Cell TransplantationJohns Hopkins All Children's HospitalNULLRecruitingN/A21 YearsAll17Phase 2United States

65. 原発性免疫不全症候群


臨床試験数 : 482 薬物数 : 653 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 212
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04414046
(ClinicalTrials.gov)
July 22, 202024/5/2020TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Primary Immunodeficiency and Inherited Metabolic Disorders in ChildrenStudy of TCR Alpha Beta T-Cell and CD19 B-Cell Depletion for Hematopoietic Cell Transplantation From Haploidentical Donors in the Treatment of Primary Immunodeficiency and Inherited Metabolic Disorders in ChildrenPrimary Immune Deficiency Disorders;Metabolic DiseaseBiological: Haploidentical Hematopoietic Cell TransplantationJohns Hopkins All Children's HospitalNULLRecruitingN/A21 YearsAll17Phase 2United States