Lentiviral vector transduced CD34+ cells ( DrugBank: - )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
65	原発性免疫不全症候群	2

65. 原発性免疫不全症候群

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臨床試験数 : 482 /  薬物数 : 653 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 212

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03601286 (ClinicalTrials.gov)	December 21, 2018	22/2/2018	Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency	Phase I/II Study of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan	Severe Combined Immunodeficiency, X-Linked	Drug: Lentiviral vector transduced CD34+ cells	Great Ormond Street Hospital for Children NHS Foundation Trust	NULL	Recruiting	8 Weeks	5 Years	Male	5	Phase 1	United Kingdom
2	NCT02234934 (ClinicalTrials.gov)	October 29, 2015	4/9/2014	Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease	A Two-Part, Phase I/II, Non Randomized, Multicenter, Open-Label Study of G1XCGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease	Granulomatous Disease, Chronic, X-linked	Biological: Lentiviral G1XCGD Gene Therapy	University of California, Los Angeles	Boston Children's Hospital;National Heart, Lung, and Blood Institute (NHLBI);Genethon;California Institute for Regenerative Medicine (CIRM)	Recruiting	23 Months	N/A	Male	16	Phase 1/Phase 2	United States