Vyondys 53 ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
113Muscular dystrophy1

113. Muscular dystrophy


Clinical trials : 622 Drugs : 485 - (DrugBank : 99) / Drug target genes : 59 - Drug target pathways : 168
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agemin
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PhaseCountries
1NCT04708314
(ClinicalTrials.gov)
October 31, 202021/9/2020An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyAn Open-Label Study to Evaluate the Safety of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyDrug: Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]Rare Disease Research, LLCSarepta Therapeutics, Inc.Terminated7 YearsN/AMale2Phase 4United States