240. Phenylketonuria
125 clinical trials, 95 drugs (DrugBank: 11 drugs), 1 drug target gene, 5 drug target pathways
Other name(s) = "PKU", "Phenylalanine hydroxylase deficiency", "PAH deficiency", "Tetrahydrobiopterin deficiency", "BH4 deficiency", "BH4 reactive hyper pheemia"