244. メープルシロップ尿症
［臨床試験数：1，薬物数：1（DrugBank：1），標的遺伝子数：0，標的パスウェイ数：0］
Searched query = "Maple syrup urine disease", "MSUD"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT01529060 (ClinicalTrials.gov) | February 2013 | 6/2/2012 | Phenylbutyrate Therapy for Maple Syrup Urine Disease | A Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine Disease | Maple Syrup Urine Disease | Drug: Phenylbutyrate;Drug: Placebo powder | Brendan Lee | NULL | Completed | 3 Years | N/A | All | 20 | Phase 2;Phase 3 | United States |