DDrare: Database of Drug Development for Rare Diseases

302. レーベル遺伝性視神経症
［臨床試験数：20，薬物数：14（DrugBank：4），標的遺伝子数：5，標的パスウェイ数：32］

Searched query = "Leber hereditary optic neuropathy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Drug = Béfizal; Cyclosporine; GS010; Genetic: GS010; Idebenone; Lenadogene nolparvovec; NADH; PENDING; Pending; RAAV2-ND4; RAAV2/2-ND4 VECTOR; Recombinant AAV vector serotype 2 containing the human wild type mitochondrial ND4 gene; Recombinant Adeno-Associated Viral vector, serotype 2 (rAAV2/2) containing the human wild-type mitochondrial NADH Dehydrogenase 4 gene (ND4); VA

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02176733 (ClinicalTrials.gov)	July 2011	25/6/2014	Trial of Cyclosporine in the Acute Phase of Leber Hereditary Optic Neuropathy		Leber Hereditary Optic Neuropathy	Drug: cyclosporine	University Hospital, Angers	NULL	Recruiting	18 Years	N/A	Both	12	Phase 2	France

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT02176733
(ClinicalTrials.gov)

July 2011

25/6/2014

Trial of Cyclosporine in the Acute Phase of Leber Hereditary Optic Neuropathy

Leber Hereditary Optic Neuropathy

Drug: cyclosporine

University Hospital, Angers

NULL

Recruiting

18 Years

N/A

Both

Phase 2

France