DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
233	ウォルフラム症候群	1

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03717909 (ClinicalTrials.gov)	December 28, 2018	11/10/2018	Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome	A Pivotal, International, Randomised, Double-blind, Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome	Wolfram Syndrome	Drug: Sodium Valproate 200Mg E/C Tablet;Drug: Sodium Valproate matched placebo	University of Birmingham	NULL	Recruiting	5 Years	N/A	All	70	Phase 2	France;Poland;Spain;United Kingdom

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT03717909
(ClinicalTrials.gov)

December 28, 2018

11/10/2018

Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome

A Pivotal, International, Randomised, Double-blind, Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome

Wolfram Syndrome

Drug: Sodium Valproate 200Mg E/C Tablet;Drug: Sodium Valproate matched placebo

University of Birmingham

NULL

Recruiting

5 Years

N/A

All

Phase 2

France;Poland;Spain;United Kingdom