Rtx-134    (DrugBank: -)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
240フェニルケトン尿症1

240. フェニルケトン尿症 [臨床試験数:125,薬物数:95(DrugBank:11),標的遺伝子数:1,標的パスウェイ数:5
Searched query = "Phenylketonuria", "PKU", "Phenylalanine hydroxylase deficiency", "PAH deficiency", "Tetrahydrobiopterin deficiency", "BH4 deficiency", "BH4 reactive hyper pheemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 125 trial found
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PhaseCountries
1NCT04110496
(ClinicalTrials.gov)
January 29, 202023/9/2019Safety and Tolerability of RTX-134 in Adults With PhenylketonuriaA Phase 1b Open-Label Single Dose Safety, Tolerability, and Pharmacokinetics Study of RTX-134 in Adults With PhenylketonuriaPhenylketonuriasDrug: RTX-134Rubius TherapeuticsNULLActive, not recruiting18 YearsN/AAll12Phase 1United States