DDrare: Database of Drug Development for Rare Diseases

Active bmn 111: daily subcutaneous injection of 15 ug/kg of bmn 111 (DrugBank: -)

告示番号	疾患名（ページ内リンク）	臨床試験数
276	軟骨無形成症	1

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03989947 (ClinicalTrials.gov)	June 12, 2019	22/5/2019	An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia	A Phase 2 Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children With Achondroplasia	Achondroplasia	Drug: Active BMN 111: Daily subcutaneous injection of 15 ug/kg of BMN 111	BioMarin Pharmaceutical	NULL	Enrolling by invitation	15 Months	N/A	All	70	Phase 2	United States;Australia;Japan;United Kingdom

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

June 12, 2019

22/5/2019

An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia

A Phase 2 Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children With Achondroplasia

Achondroplasia

Drug: Active BMN 111: Daily subcutaneous injection of 15 ug/kg of BMN 111

BioMarin Pharmaceutical

NULL

Enrolling by invitation

15 Months

N/A

All

Phase 2

United States;Australia;Japan;United Kingdom