DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
3	脊髄性筋萎縮症	1

告示番号

疾患名（ページ内リンク）

臨床試験数

脊髄性筋萎縮症

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02644668 (ClinicalTrials.gov)	January 14, 2016	23/12/2015	A Study of CK-2127107 in Patients With Spinal Muscular Atrophy	A Phase 2, Double-Blind, Randomized, Placebo-Controlled, Multiple Dose Study of CK-2127107 in Two Ascending Dose Cohorts of Patients With Spinal Muscular Atrophy	Spinal Muscular Atrophy	Drug: Placebo;Drug: Reldesemtiv 150 mg;Drug: Reldesemtiv 450 mg	Cytokinetics	Astellas Pharma Global Development, Inc.	Completed	12 Years	N/A	All	70	Phase 2	United States;Canada

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT02644668
(ClinicalTrials.gov)

January 14, 2016

23/12/2015

A Study of CK-2127107 in Patients With Spinal Muscular Atrophy

A Phase 2, Double-Blind, Randomized, Placebo-Controlled, Multiple Dose Study of CK-2127107 in Two Ascending Dose Cohorts of Patients With Spinal Muscular Atrophy

Spinal Muscular Atrophy

Drug: Placebo;Drug: Reldesemtiv 150 mg;Drug: Reldesemtiv 450 mg

Cytokinetics

Astellas Pharma Global Development, Inc.

Completed

12 Years

N/A

All

Phase 2

United States;Canada