245. Propionic acidemia Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 13 Drugs : 16 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 6

Drugs and their primary sponsors and trial info
BBP-671   
   CoA Therapeutics, Inc., a BridgeBio company
      2021   Phase 1   NCT04836494   United States;
CX-016492   
   ModernaTX, Inc
      2020   Phase 1;Phase 2   EUCTR2019-003529-36-GB   Canada;United Kingdom;United States;
CX-017950   
   ModernaTX, Inc
      2020   Phase 1;Phase 2   EUCTR2019-003529-36-GB   Canada;United Kingdom;United States;
Carbaglu   
   Mendel Tuchman
      2012   Phase 2   NCT01599286   United States;
Carglumic Acid (Carbaglu®)   
   National Taiwan University Hospital
      2019   -   NCT04284917   Taiwan;
Disodium citrate   
   Nicola Longo
      2008   Phase 1   NCT00645879   United States;
Glutamine   
   Nicola Longo
      2008   Phase 1   NCT00645879   United States;
HST5040   
   HemoShear Therapeutics
      2021   Phase 2   NCT04732429   United States;
MRNA-3927   
   ModernaTX, Inc
      2020   Phase 1;Phase 2   EUCTR2019-003529-36-GB   Canada;United Kingdom;United States;
   ModernaTX, Inc.
      2021   Phase 1/Phase 2   NCT05130437   Canada;United Kingdom;United States;
      2021   Phase 1/Phase 2   NCT04159103   Canada;United Kingdom;United States;
Ornithine alpha ketoglutarate   
   Nicola Longo
      2008   Phase 1   NCT00645879   United States;