286. Hereditary sideroblastic anemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 7 / Drugs : 20 - (DrugBank : 10) / Drug target genes : 8 - Drug target pathways : 43
Drugs and their primary sponsors and trial info
ALA
Department of Hematolgy and Rheumatology, Tohoku University Graduate School of Medicine
2016 - JPRN-UMIN000023490 Japan;
Allogeneic Bone Marrow Transplantation
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Aminolevulinic acid
Department of Hematology and Oncology, Graduate School of Medicine, Kyoto University
2016 - JPRN-UMIN000021407 Japan;
DEFEROXAMINE MESILATE
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
DFO
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Deferasirox
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Deferoxamine
NOVARTIS FARMA
2010 - EUCTR2010-021062-29-IT Greece;Italy;United Kingdom;
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Desferal
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
EXJADE
NOVARTIS FARMA
2010 - EUCTR2010-021062-29-IT Greece;Italy;United Kingdom;
Exjade
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
Fludarabine Phosphate
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
ICL670
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Methotrexate
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Peripheral Blood Stem Cell Transplantation
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Phosphate
Department of Hematolgy and Rheumatology, Tohoku University Graduate School of Medicine
2016 - JPRN-UMIN000023490 Japan;
Department of Hematology and Oncology, Graduate School of Medicine, Kyoto University
2016 - JPRN-UMIN000021407 Japan;
Tacrolimus
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Treosulfan
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Department of Hematolgy and Rheumatology, Tohoku University Graduate School of Medicine
2016 - JPRN-UMIN000023490 Japan;
Allogeneic Bone Marrow Transplantation
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Aminolevulinic acid
Department of Hematology and Oncology, Graduate School of Medicine, Kyoto University
2016 - JPRN-UMIN000021407 Japan;
DEFEROXAMINE MESILATE
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
DFO
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Deferasirox
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Deferoxamine
NOVARTIS FARMA
2010 - EUCTR2010-021062-29-IT Greece;Italy;United Kingdom;
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Desferal
Novartis Pharma Services AG
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
EXJADE
NOVARTIS FARMA
2010 - EUCTR2010-021062-29-IT Greece;Italy;United Kingdom;
Exjade
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
Fludarabine Phosphate
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
ICL670
Novartis Pharma Services AG
2011 - EUCTR2010-021062-29-GR Greece;Italy;United Kingdom;
2010 - EUCTR2010-021062-29-GB Greece;Italy;United Kingdom;
2008 Phase 2 EUCTR2007-000766-20-GB Italy;United Kingdom;
Methotrexate
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Peripheral Blood Stem Cell Transplantation
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Phosphate
Department of Hematolgy and Rheumatology, Tohoku University Graduate School of Medicine
2016 - JPRN-UMIN000023490 Japan;
Department of Hematology and Oncology, Graduate School of Medicine, Kyoto University
2016 - JPRN-UMIN000021407 Japan;
Tacrolimus
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;
Treosulfan
Fred Hutchinson Cancer Research Center
2022 Phase 2 NCT04965597 United States;