324. Methylglutaconic aciduria Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 4 Drugs : 4 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10

Drugs and their primary sponsors and trial info
Bezafibrate (INN 3968)   
   University Hospitals Bristol NHS Foundation Trust
      2019   Phase 2   EUCTR2015-001382-10-GB   United Kingdom;
Elamipretide   
   Stealth BioTherapeutics Inc.
      2020   -   NCT04689360   -
      2017   Phase 2/Phase 3   NCT03098797   United States;
Triheptanoin   
   Jerry Vockley, MD, PhD
      2009   -   NCT01461304   United States;