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 255. 複合カルボキシラーゼ欠損症 [臨床試験数:1,薬物数:1(DrugBank:0),標的遺伝子数:0,標的パスウェイ数:0] 

Searched query = "Multiple carboxylase deficiency", "Holocarboxylase synthetase deficiency", "HCS deficiency", "Biotinidase deficiency"
The queries were searched in Public_title, Scientific_title, and Condition of the data. Export date: 11/21/2019. Trials are sorted by Date_enrolment from most recent to oldest in the table.

Search in Page    e.g. "Phase 3", "Not recruiting", "Japan"    Synonyms (DrugBank) were also searched for.
No.TrialIDDate_
enrollement
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Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
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PhaseCountries
1NCT03269045August 31, 201322 January 2018Study of ORL-1B in Patients With Biotinidase DeficiencyAn Open-label, Single-arm, Phase 2 Study of ORL-1B in Patients With Biotinidase DeficiencyBiotinidase DeficiencyDrug: ORL-1BOrpha LabsNot recruitingN/A18 YearsAll20Phase 1/Phase 2