21. Mitochondrial disease
23 clinical trials,   29 drugs   (DrugBank: 28 drugs),   44 drug target genes,   65 drug target pathways
Searched query = "Mitochondrial disease"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT00060515 (ClinicalTrials.gov) | April 2003 | 7/5/2003 | RG2133 (2',3',5'-Tri-O-Acetyluridine) in Mitochondrial Disease | An Open-Label Dose-Escalation Phase I Study to Asses the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of RG2133 (2',3',5'-Tri-O-Acetyluridine) in the Treatment of Inherited Mitochondrial Diseases | Mitochondrial Diseases | Drug: RG2133 (2',3',5'-tri-O-acetyluridine) | Repligen Corporation | NULL | Terminated | 3 Years | N/A | Both | 12 | Phase 1 | United States |