19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 /  薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

  
2 trials found
No.TrialIDDate_
enrollment		Date_
registration		Public_titleScientific_titleConditionInterventionPrimary_
sponsor		Secondary_
sponsor		Recruitment_
Status		Inclusion_
agemin		Inclusion_
agemax		Inclusion_
gender		Target_
size		PhaseCountries
1NCT05629559
(ClinicalTrials.gov)		October 16, 20224/11/20224D-310 in Adults With Fabry Disease and Cardiac InvolvementAn Open-Label, Phase 1/2a Trial of Gene Therapy 4D-310 in Adults With Fabry Disease and Cardiac InvolvementFabry DiseaseBiological: 4D-3104D Molecular TherapeuticsNULLActive, not recruiting18 YearsN/AAll18Phase 1/Phase 2Australia;Taiwan
2NCT04519749
(ClinicalTrials.gov)		September 1, 202014/8/2020An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry DiseaseAn Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry DiseaseFabry DiseaseBiological: 4D-3104D Molecular TherapeuticsNULLActive, not recruiting18 YearsN/AAll18Phase 1/Phase 2United States