19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

  
1 trial found
No.TrialIDDate_
enrollment
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agemin
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PhaseCountries
1NCT02455622
(ClinicalTrials.gov)
October 28, 201520/5/2015Long-term Evaluation on Height and Weight in Patients With MPS II Who Started Treatment at < 6 Years of AgeA Long-Term, Open-Label, Multicenter, Phase IV Study to Assess Longitudinal Changes on Height and Weight in Patients With MPS II Who Are Receiving Elaprase and Started Treatment With Elaprase at <6 Years of AgeHunter SyndromeDrug: Elaprase for intravenous (IV) infusionTakedaTakeda Development Center Americas, Inc.Active, not recruitingN/A6 YearsMale21Phase 4United States;Dominican Republic;Germany;Malaysia;Philippines;Serbia;Thailand;Vietnam;Oman;Saudi Arabia