19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

  
3 trials found
No.TrialIDDate_
enrollment
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Public_titleScientific_titleConditionInterventionPrimary_
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agemin
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agemax
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PhaseCountries
1NCT02124070
(ClinicalTrials.gov)
March 26, 201425/4/2014Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of CystinosisTherapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of CystinosisCystinosis;MyopathyDrug: rh Growth HormoneNational Human Genome Research Institute (NHGRI)NULLWithdrawn18 Years70 YearsAll0Phase 1/Phase 2United States
2NCT00748969
(ClinicalTrials.gov)
November 20088/9/2008Clinical Trial of Growth Hormone in MPS I, II, and VIPhase II/III, Randomized, Clinical Trial of the Effects of Nutropin AQ® on Growth and Bone Metabolism in Children With MPS I, II, and VI and Short StatureMucopolysaccharidosis I;Mucopolysaccharidosis II;Mucopolysaccharidosis VIDrug: Somatropin (DNA origin)Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical CenterNULLTerminated5 Years17 YearsAll2Phase 2/Phase 3United States
3NCT00286689
(ClinicalTrials.gov)
February 3, 20061/2/2006Effects of Growth Hormone in Chronically Ill ChildrenHurler Syndrome;Cerebral Palsy;Juvenile Rheumatoid Arthritis;Crohn Disease;HIV InfectionsDrug: Growth Hormone;Procedure: Whole body Protein turnover;Procedure: DEXA scanUniversity of Texas Southwestern Medical CenterNULLWithdrawn3 Years17 YearsAll0N/AUnited States