256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details
臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03045042 (ClinicalTrials.gov) | April 2017 | 27/1/2017 | Search for Serum/Plasma Biomarkers in Pompe's Disease | Search for Serum/Plasma Biomarkers in Pompe's Disease | Late Onset Pompe Disease;Pompe Disease | Drug: Enzyme Replacement Agent | Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau | Genzyme, a Sanofi Company | Not yet recruiting | 2 Years | N/A | All | 35 | N/A | Spain |