256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details
臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04120168 (ClinicalTrials.gov) | April 1, 2019 | 7/10/2019 | Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease | Multicenter Non-Drug Screening Study to Determine the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease in Children With Unexplained Transaminase Elevation | Duchenne Muscular Dystrophy;Pompe Disease (Late-onset) | Genetic: Laboratory Tests | Turkish Society of Pediatric Gastroenterology, Hepatology and Nutrition | NULL | Completed | 3 Months | 18 Years | All | 590 | Turkey |