251. Urea cycle disorder Clinical trials / Disease details


Clinical trials : 54 Drugs : 61 - (DrugBank : 15) / Drug target genes : 3 - Drug target pathways : 28

  
1 trial found
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1NCT00004386
(ClinicalTrials.gov)
October 199518/10/1999Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseGenetic: recombinant adenovirus containing the ornithine transcarbamylase geneEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Children's Research InstituteTerminated18 Years65 YearsBothPhase 1NULL