Elosulfase alfa ( DrugBank: Elosulfase alfa )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
19ライソゾーム病2

19. ライソゾーム病


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03204370
(ClinicalTrials.gov)
February 1, 20187/6/2017Natural History of Atypical Morquio A DiseaseNatural History of Atypical Morquio A Disease: a 5-years Prospective Study in a Series of 9 Adult Patients Followed in a Single Expert CenterMucopolysaccharidosis IV ADrug: Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]GOIZETBioMarin PharmaceuticalActive, not recruiting18 YearsN/AAll10France
2NCT02294877
(ClinicalTrials.gov)
September 201428/10/2014A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)Mucopolysaccharidosis IV Type A;Morquio A Syndrome;MPS IVADrug: Vimizim® (elosulfase alfa)BioMarin PharmaceuticalICON plcActive, not recruitingN/AN/AAll425United States;Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Ireland;Italy;Malaysia;Netherlands;Poland;Portugal;Puerto Rico;Taiwan;United Kingdom;Germany