FLT201 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
19ライソゾーム病1

19. ライソゾーム病


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT05324943
(ClinicalTrials.gov)
April 15, 202228/2/2022A Gene Therapy Study in Patients With Gaucher Disease Type 1A Phase 1/2, Open-label, Safety, Tolerability, and Efficacy Study of FLT201 in Adult Patients With Gaucher Disease Type 1 (GALILEO-1)Gaucher Disease, Type 1Genetic: FLT201Freeline TherapeuticsNULLRecruiting18 YearsN/AAll18Phase 1/Phase 2Argentina;Brazil;Germany;Israel;Paraguay;Spain;United Kingdom;Italy;Tunisia