Gene-modified autologous stem cells ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
285ファンコニ貧血1

285. ファンコニ貧血


臨床試験数 : 62 薬物数 : 93 - (DrugBank : 30) / 標的遺伝子数 : 30 - 標的パスウェイ数 : 144
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03351868
(ClinicalTrials.gov)
December 1, 201720/11/2017FANCA Gene Transfer for Fanconi Anemia Using a High-safety, High-efficiency, Self-inactivating Lentiviral VectorGene Transfer for Fanconi Anemia Using a Self-inactivating Lentiviral VectorFanconi AnemiaGenetic: Gene-modified autologous stem cellsShenzhen Geno-Immune Medical InstituteNULLRecruiting2 Years20 YearsAll10N/AChina