Fordadistrogene movaparvovec ( DrugBank: Fordadistrogene movaparvovec )


1 disease
IDDisease name (Link within this page)Number of trials
113Muscular dystrophy2

113. Muscular dystrophy


Clinical trials : 646 Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170
No.TrialIDDate_
enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT05689164
(ClinicalTrials.gov)
April 14, 20239/1/2023A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.Long-term Follow-up Safety and Efficacy Study in Participants With Duchenne Muscular Dystrophy Who Have Received Fordadistrogene Movaparvovec in a Preceding Clinical StudyDuchenne Muscular DystrophyBiological: fordadistrogene movaparvovecPfizerNULLNot yet recruiting0 YearsN/AMale250Phase 3NULL
2NCT05429372
(ClinicalTrials.gov)
August 8, 20228/10/2021Study of Fordadistrogene Movaparvovec in Early Stage Duchenne Muscular DystrophyA PHASE 2, MULTICENTER, SINGLE-ARM STUDY TO EVALUATE THE SAFETY AND DYSTROPHIN EXPRESSION AFTER FORDADISTROGENE MOVAPARVOVEC (PF-06939926) ADMINISTRATION IN MALE PARTICIPANTS WITH EARLY STAGE DUCHENNE MUSCULAR DYSTROPHYMuscular Dystrophy, DuchenneGenetic: PF-06939926PfizerNULLRecruiting2 Years3 YearsMale10Phase 2United States;Australia