Alpelisib ( DrugBank: Alpelisib )


1 disease
IDDisease name (Link within this page)Number of trials
138Nerve cell migration disorder1

138. Nerve cell migration disorder


Clinical trial : 1 Drugs : 2 - (DrugBank : 1) / Drug target gene : 1 - Drug target pathways : 106
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enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT05577754
(ClinicalTrials.gov)
November 28, 202210/10/2022Assessment of the Efficacy and Safety of Alpelisib (BYL719) in Pediatric and Adult Patients With Megalencephaly-CApillary Malformation Polymicrogyria Syndrome (MCAP)A Phase II Double-blind Multi-center, Placebo-controlled Trial, to Assess the Efficacy and Safety of Alpelisib (BYL719) in Pediatric and Adult Patients With Megalencephaly-CApillary Malformation Polymicrogyria Syndrome (MCAP)Megalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP)Drug: Alpelisib (BYL719);Drug: Matching placebo;Procedure: Optional lumbar punctureCentre Hospitalier Universitaire DijonNULLRecruiting2 Years40 YearsAll16Phase 2France