240. Phenylketonuria
125 clinical trials,   95 drugs   (DrugBank: 11 drugs),   1 drug target gene,   5 drug target pathways

Searched query = "Phenylketonuria", "PKU", "Phenylalanine hydroxylase deficiency", "PAH deficiency", "Tetrahydrobiopterin deficiency", "BH4 deficiency", "BH4 reactive hyper pheemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
1 trial found
No.TrialIDDate_
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agemin
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PhaseCountries
1NCT04110496
(ClinicalTrials.gov)
January 29, 202023/9/2019Safety and Tolerability of RTX-134 in Adults With PhenylketonuriaA Phase 1b Open-Label Single Dose Safety, Tolerability, and Pharmacokinetics Study of RTX-134 in Adults With PhenylketonuriaPhenylketonuriasDrug: RTX-134Rubius TherapeuticsNULLActive, not recruiting18 YearsN/AAll12Phase 1United States