263. Cerebrotendinous xanthomatosis
5 clinical trials, 10 drugs (DrugBank: 2 drugs), 2 drug target genes, 4 drug target pathways
Searched query = "Cerebrotendinous xanthomatosis", "27-hydroxylase deficiency", "CYP27 deficiency"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | JPRN-JapicCTI-205157 | 03/8/2020 | 13/02/2020 | An open-label study of FPF1011 in patients with cerebrotendinous xanthomatosis (phase 3) | An open-label study of FPF1011 in patients with cerebrotendinous xanthomatosis (phase 3) | Cerebrotendinous xanthomatosis | Intervention name : FPF1011 INN of the intervention : Chenodeoxycholic acid Dosage And administration of the intervention : Dose of chenodeoxycholic acid is 750 mg/day for patients aged 20 or older, and 15 mg/kg/day under ages 20, administered orally in three divided doses a day. Control intervention name : - INN of the control intervention : - Dosage And administration of the control intervention : - | Fujimoto Pharmaceutical Corporation | NULL | recruiting | 0 | BOTH | 5 | Phase 3 | Japan |