284. Diamond-Blackfan anemia
37 clinical trials,   110 drugs   (DrugBank: 34 drugs),   22 drug target genes,   121 drug target pathways

Searched query = "Diamond-Blackfan anemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
2 trials found
No.TrialIDDate_
enrollment
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Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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agemax
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PhaseCountries
1NCT02386267
(ClinicalTrials.gov)
September 201418/2/2015L-leucine in Diamond Blackfan Anemia PatientsTherapeutic Use of the Amino Acid Leucine in the Treatment of Transfusion-Dependent Diamond Blackfan Anemia PatientsDiamond Blackfan AnemiaDrug: L-leucineFederal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry RogacheNULLRecruiting1 Year20 YearsBoth30Phase 2Russian Federation
2NCT01362595
(ClinicalTrials.gov)
June 201320/5/2011Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan AnemiaThe Use of Novel Therapies to Reconstitute Blood Cell Production and Promote Organ Performance Using Bone Marrow Failure as a Model: a Pilot, Phase I/II Study of the Amino Acid Leucine in the Treatment of Patients With Transfusion-Dependent Diamond Blackfan AnemiaDiamond Blackfan Anemia;Blackfan Diamond Syndrome;DBA;Congenital Hypoplastic Anemia;Pure Red Cell AplasiaDrug: leucineNorthwell HealthNULLActive, not recruiting2 YearsN/AAll50Phase 1;Phase 2United States